Ongoing (Closed To New Participants)


  • Expanded Access Protocol for Boys with Duchenne Muscular Dystrophy

    Brief Description: For details, please refer to https://www.clinicaltrials.gov/ct2/show/NCT03863119
    Sponsor: Santhera Pharmaceuticals (Switzerland) Ltd. (Formerly ReveraGen)
  • Sleep Efficiency in Boys with DMD and their Caregivers

    Brief Description:
    This study requests boys with Duchenne Muscular Dystrophy and their caregivers/parents to wear the ActiGraph GT9x, a wrist-worn portable fitness tracking device, to objectively explore sleep factors, such as amount of time to achieve sleep, time in various levels of sleep, overall awake times, and movement during the night. In addition, boys with DMD will wear the ActiGraph throughout the day to record daily activity. To learn more about the study eligibility please contact Dr. Roxanna Bendixen (bendixen@pitt.edu).