Recruiting


  • Community Based Outcome Measures in Boys with DMD

    Brief Description: Participants are being invited to take part in this parallel research study if they are enrolled in VBP15 2b clinical trial for boys with Duchenne Muscular Dystrophy (DMD). This study requests boys enrolled in VBP 15 wear the ActiGraph GT9x, a wrist-worn portable fitness tracking device, to objectively explore sleep factors and daily physical activity throughout the clinical trial. Patient reported outcomes regarding sleep and daily participation will also be collected. To learn more about the study eligibility please contact Dr. Roxanna Bendixen (bendixen@pitt.edu).
  • Sleep Efficiency in Boys with DMD and their Caregivers

    Brief Description:
    This study requests boys with Duchenne Muscular Dystrophy and their caregivers/parents to wear the ActiGraph GT9x, a wrist-worn portable fitness tracking device, to objectively explore sleep factors, such as amount of time to achieve sleep, time in various levels of sleep, overall awake times, and movement during the night. In addition, boys with DMD will wear the ActiGraph throughout the day to record daily activity. To learn more about the study eligibility please contact Dr. Roxanna Bendixen (bendixen@pitt.edu).
  • A Phase IIb Randomized, Double-blind, Parallel Placebo- and Active-controlled Study to Assess the Efficacy and Safety of Vamorolone in Ambulatory Boys with Duchenne Muscular Dystrophy (DMD)

    Brief Description: The study is a Phase IIb randomized, double-blind, parallel group, placebo and active-controlled study to evaluate the efficacy, safety, and pharmacodynamics of vamorolone in boys with DMD. To learn more about the study eligibility and participating sites, please contact us at info@trinds.com.
    Sponsor: ReveraGen