A Phase IIa, Open-Label, Multiple Ascending Dose Study to Assess the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Exploratory Efficacy of Vamorolone in Boys with Duchenne Muscular Dystrophy (DMD)

This study is evaluating the safety and tolerability of a new steroid-like intervention called Vamorolone in boys with DMD ages 4 to less than 7 years old. Approximately 48 patients will be enrolled in participating sites in the United States, Canada, Australia, Israel, Sweden, and the United Kindgom. To learn more about the study eligibility and participating sites please visit: https://clinicaltrials.gov/ct2/show/NCT02760264 or contact us at info@trinds.com.